Awards Grant
- Combination therapy to improve on CuATSM outcomes in ALS
- Enhancing delivery of gene therapy to motor neurons and glial cells using focused ultrasound
- Prion-like strains of TDP-43 aggregates in MND and FTLD
- Restoring autoregulation of TDP43 in sporadic amyotrophic lateral sclerosis using splice-switching antisense oligonucleotides
- Targeting misfolded proteins with MisfoldUbLs as a therapeutic strategy for ALS
- Using patient derived cells to define an electrical signature of sporadic ALS and to develop a high throughput drug screening technology and novel therapy